congenital myasthenia
Showing 1 - 25 of 2,029
Congenital Myasthenic Syndrome Trial in Sacramento (3,4-Diaminopyridine)
Available
- Congenital Myasthenic Syndrome
-
Sacramento, CaliforniaUniversity of California, Davis Medical Center
Apr 18, 2022
Exercise in Autoimmune Myasthenia Gravis and Myasthenic
Completed
- Autoimmune Myasthenia Gravis
- +3 more
-
Paris, FranceOnline Questionnaire
Jun 3, 2022
Lambert-Eaton Myasthenic Syndrome (LEMS), Congenital Myasthenia (CM) Trial in Portland (3,4-diaminopyridine)
No longer available
- Lambert-Eaton Myasthenic Syndrome (LEMS)
- Congenital Myasthenia (CM)
-
Portland, OregonOregon Health & Science University
Dec 9, 2019
Rare Disorders, Undiagnosed Disorders, Disorders of Unknown Prevalence Trial in Sioux Falls, Sydney
Recruiting
- Rare Disorders
- +309 more
-
Sioux Falls, South Dakota
- +1 more
Jun 20, 2022
Generalized Myasthenia Gravis Trial (rozanolixizumab)
Not yet recruiting
- Generalized Myasthenia Gravis
- (no location specified)
Nov 28, 2023
Participants With DOK7 Congenital Myasthenic Syndromes (CMS)
Not yet recruiting
- Congenital Myasthenic Syndrome
- (no location specified)
Oct 9, 2023
Generalized Myasthenia Gravis Trial (zilucoplan (RA101495))
Not yet recruiting
- Generalized Myasthenia Gravis
- zilucoplan (RA101495)
- (no location specified)
Aug 22, 2022
Vaccination Against COVID-19 in Neuromuscular Patients
Recruiting
- Neuromuscular Diseases
- Survey
-
Bordeaux, FranceCHU de Bordeaux
Apr 1, 2022
Generalized Myasthenia Gravis Trial in Canada, United States (zilucoplan (RA101495), Placebo)
Completed
- Generalized Myasthenia Gravis
- zilucoplan (RA101495)
- Placebo
-
Mobile, Alabama
- +29 more
Jul 26, 2022
Myasthenic Syndromes, Congenital Trial in Durham (3,4-diaminopyridine)
No longer available
- Myasthenic Syndromes, Congenital
-
Durham, North CarolinaDuke University Hospital
Jan 3, 2022
Unrecognized Condition Trial in Cairo (Frontalis flap)
Completed
- Unrecognized Condition
- Frontalis flap
-
Cairo, EgyptKasr al ainy
Apr 27, 2022
Generalized Myasthenia Gravis Trial in Worldwide (M281, Placebo)
Myasthenia Gravis Trial in Guangzhou (Body fluid diagnosis)
Enrolling by invitation
- Myasthenia Gravis
- Body fluid diagnosis
-
Guangzhou, Guangdong, ChinaFirst Affiliated Hospital of Jinan University
May 25, 2023
Myasthenia Gravis Trial in New Haven (Blood Sample Draw)
Recruiting
- Myasthenia Gravis
- Blood Sample Draw
-
New Haven, ConnecticutYale-New Haven Hospital
Nov 14, 2022
Measures Pilot Trial for Telehealth in Myasthenia Gravis
Completed
- Myasthenia Gravis
- Telehealth
-
New Haven, Connecticut
- +4 more
Jun 14, 2023
Myasthenia Gravis Trial in Leiden (Pyridostigmine, Amifampridine (base) with modified release, Placebo)
Recruiting
- Myasthenia Gravis
- Pyridostigmine
- +2 more
-
Leiden, South-Holland, NetherlandsLeiden University Medical Center
Jun 16, 2023
Myasthenia Gravis Trial in United States (Blood sample)
Recruiting
- Myasthenia Gravis
- Blood sample
-
Irvine, California
- +9 more
Aug 14, 2023
Myasthenia Gravis, Generalized Trial in Worldwide (Placebo, CFZ533)
Completed
- Myasthenia Gravis, Generalized
- Placebo
- CFZ533
-
Montreal, Quebec, Canada
- +14 more
Dec 9, 2020
Myasthenia Gravis, Generalized Trial in China (Telitacicept, Placebo)
Not yet recruiting
- Myasthenia Gravis, Generalized
- Telitacicept
- Placebo
-
Bengbu, Anhui, China
- +50 more
Feb 12, 2023
Myasthenia Gravis, Generalized Trial in China (Tocilizumab Injection)
Enrolling by invitation
- Myasthenia Gravis, Generalized
- Tocilizumab Injection
-
Beijing, Beijing, China
- +5 more
Jan 27, 2023
Generalized Myasthenia Gravis, Myasthenia Gravis Trial in Worldwide (ALXN2050, Placebo)
Recruiting
- Generalized Myasthenia Gravis
- Myasthenia Gravis
- ALXN2050
- Placebo
-
Phoenix, Arizona
- +45 more
Dec 15, 2022